POSTS TAGGED AS gene therapy

Human Clinical Trials for CRISPR Underway in the US

CRISPR Cas9
Seven years after CRISPR-Cas9 gene editing appeared, clinical trials have begun.  The University of Pennsylvania has treated two patients, [MORE]

Gene Editing with CRISPR-Cas14

Gene editing
The founder of Mammoth Biosciences (South San Francisco, CA) explains in this piece the advantages of using the Cas-14 [MORE]

Gene Therapy for X-SCID

David Vetter poses inside of his bubble
David Vetter (1971-1984), aka “the Boy in the Bubble,” lived with and died from [MORE]

Prospects for CRISPR in the Clinic

Ex vivo CRISPR infographic
It is now more than a quarter century since the first authorized gene therapy clinical trial took [MORE]

A Gene and Cell Therapy “Factory” in Houston

Gene Therapy
Following closely on the news that the world’s first commercial factory (30,000 sq. ft.) for the production of induced [MORE]

Gene Therapy for Adrenoleukodystrophy

ABCD1 Gene Defect in ALD
You may remember Lorenzo Odono and the 1992 movie, “Lorenzo’s Oil,” about his and his family’s [MORE]

Altering Gene Expression with Gold Nanorods and a NIR Laser

Gold Nanorods
Japanese scientists have used lipid coated gold nanorods to deliver a gene vector, which when heated with a near [MORE]

CRISPR Skin Grafts Instead of Insulin Injections

Gene Therapy Via Skin
Researchers at the University of Chicago have used CRISPR gene editing to establish proof of concept in [MORE]

CRISPR-Cpf1 Gene Editing

CRISPR Cas Method
Gene editing technology known as CRISPR has only been known to science for four years, but its impact [MORE]

Nanoparticle-Enabled Gene Editing

CRISPR Delivery Mechanism
Getting CRISPR-Cas 9 molecules to their target cells without damage or off-targeting has been an obstacle for gene [MORE]

Technology Review’s List of Breakthroughs

Paralysis Stopper
Brain implants, gene therapy, and The Cell Atlas are among the ten things TR sees a technological breakthroughs this [MORE]

Gene Therapy’s Breakout

CRISPR-Cas9 Mode of Action
September 14, 1990 was the first FDA approved human clinical trial for gene therapy. The patient, then [MORE]

Lab Grown Cartilage from Stem Cells for Hip Prosthetics

Joint pain, especially from arthritis, seems to be part of the fate of aging. Artificial prosthetics offer some relief, but [MORE]

Nanoparticles Delivery Synthetic DNA in Treating Thalassemia in Lab Animals

Thalassemia
Several years ago a gene repair technique called “chimeraplasty” looked promising, though it never reached fruition. The idea was to [MORE]