POSTS TAGGED AS sickle cell disease

mRNA Loaded Lipid Nanoparticles in Gene Editing

A step toward stem cell engineering in Vivo
“Breda et al. [Children’s Hospital of Philadelphia] designed a strategy to reprogram bone [MORE]

Adenine Base Editing for Sickle Cell Disease

Base Editing Beats Other Genome Editing Strategies for Treating Sickle Cell Disease
“Base editing—the genome editing technique that alters base pairs [MORE]

Normal Blood Flow in Brain after Stem Cell Treatment for Sickle Cell Disease

HSCT Normalizes Brain Hemodynamics in Children With Sickle Cell Disease
“Children who undergo hematopoietic stem cell transplant (HSCT) for sickle cell [MORE]

Long Term Success for Gene Therapy in Sickle Cell Patients

Potential treatments for Sickle Cell Disease
“Gene therapy with the use of LentiGlobin for sickle cell disease (bb1111; lovotibeglogene autotemcel) consists [MORE]

Another Win for CRISPR

CRISPR therapy for rare blood diseases
“Back in 2019 the first CRISPR human clinical trials kicked off in the United States. [MORE]