TAG ARCHIVE

POSTS TAGGED AS adeno-associated viral vector

Gene Therapy for Arrhythmogenic Cardiomyopathy

February 13, 2024 | | Posted in Newsletter

Therapeutic efficacy of AAV-mediated restoration of PKP2 in arrhythmogenic cardiomyopathy
“Arrhythmogenic cardiomyopathy is a severe cardiac disorder characterized by lethal arrhythmias [MORE]

Single Dose Gene Therapy for Cocaine Addiction

March 17, 2020 | | Posted in Newsletter

Single dose gene therapy for cocaine addiction
In an article titled “Systemic Safety of a Recombinant AAV8 Vector for Human Cocaine [MORE]

Gene Therapy for Pulmonary Hypertension

May 17, 2016 | | Posted in Newsletter

Gene Therapy
Lung tissue is amenable to aerosol delivery of therapeutics. This piece describes how researchers at Mount Sinai School of [MORE]