ABCD1 Gene Defect in ALD
You may remember Lorenzo Odono and the 1992 movie, “Lorenzo’s Oil,” about his and his family’s [MORE]
AAV2 Ribbon Diagram
Adeno-associated virus looked like a promising vector for gene therapy in the mid-1990s, but then sank with the [MORE]
Synthesised Nanoparticles
Researchers have known for the past 25 years that the future of gene therapy depends on safer viral vectors. [MORE]
Gene therapy mainly relies on viral vectors to introduce DNR or RNA into target cells. Viruses have the advantage [MORE]
Purple Cells – New Leukemia Treatment
This piece reports a gene therapy success against chronic lymphocytic leukemia for three patients [MORE]