POSTS TAGGED AS Muscular dystrophy

50 Neuropathology Assays in One Genetic Test

Tandem repeated expression disorders
“We [researchers with the Garvan Institute of Medical Research, Sydney, Australia] describe the use of programmable targeted [MORE]

Gene Therapy for Duchenne Muscular Dystrophy

Jude Samulski PhD work in gene therapy improves outcomes for DMD
Duchenne Muscular Dystrophy was one of the early targets for [MORE]

13 Years of iPSC Therapies in Clinical Trials

iPS cell therapies for clinical trials
Thirteen years have passed since Kyoto University’s Shinya Yamanaka demonstrated how altering four genes could [MORE]

Injectable Stem Cells for Muscle Repair

Stem cell loaded hydrogel
Though the term “hydrogel” originated in the late 19th century, its modern definition as a hydrophilic crosslinked [MORE]

Gene Therapy’s Breakout

CRISPR-Cas9 Mode of Action
September 14, 1990 was the first FDA approved human clinical trial for gene therapy. The patient, then [MORE]

Electrical Impedance Myography

Myography
Using a probe and sensor approach similar to one that evaluates fat in the body, Harvard Medical School neurologist Seward [MORE]