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POSTS TAGGED AS Duchenne Muscular Dystrophy

How Patient Age, Vector Dose, and Immune Response Figure in Gene Therapy for Duchenne Muscular Dystrophy

August 8, 2023 | | Posted in Newsletter

Gene editing therapy for DMD
“Based on the finding, the researchers [Sarepta Therapeutics] identified a need for more data on the [MORE]

Muscle-Tropic Capsids for Gene Transfer

November 30, 2021 | | Posted in Newsletter

Graphical abstract
“Here, we [scientists at the Broad Institute-MIT/Harvard] developed the DELIVER (directed evolution of AAV capsids leveraging in vivo expression [MORE]

Gene Therapy for Duchenne Muscular Dystrophy

September 29, 2020 | | Posted in Newsletter

Jude Samulski PhD work in gene therapy improves outcomes for DMD
Duchenne Muscular Dystrophy was one of the early targets for [MORE]