Gene editing therapy for DMD
“Based on the finding, the researchers [Sarepta Therapeutics] identified a need for more data on the [MORE]
Graphical abstract
“Here, we [scientists at the Broad Institute-MIT/Harvard] developed the DELIVER (directed evolution of AAV capsids leveraging in vivo expression [MORE]
Jude Samulski PhD work in gene therapy improves outcomes for DMD
Duchenne Muscular Dystrophy was one of the early targets for [MORE]