TAG ARCHIVE

POSTS TAGGED AS sickle cell anemia

Clinical Success for Gene Editing, but at a Price None Could Afford

March 26, 2024 | | Posted in Newsletter

The first gene-editing treatment for Sickle Cell
“Many CRISPR treatments are in trials, but in 2022, Vertex Pharmaceuticals, based in Boston, [MORE]

One Shot Gene Therapy for Sickle Cell Disease

October 10, 2023 | | Posted in Newsletter

One Shot Gene Therapy for Sickle Cell Disease
“On July 27 in Science, scientists from Children’s Hospital of Philadelphia and the [MORE]

Gene Editing Shows Long Term Efficacy forBeta Thalassemia and Sickle Cell Disease

August 23, 2022 | | Posted in Newsletter

Sickle Cell Anemia
“In a late-breaking abstract presented at the European Hematology Association (EHA) Congress, a group of researchers that includes [MORE]

UCLA and Collaborators Create a Road Map for Blood Stem Cell Maturation

May 10, 2022 | | Posted in Newsletter

Human blood stem cells emerging from specialized endothelial cells in the wall of an embryonic aorta
“The data make it possible [MORE]

Detecting de Novo Mutations

April 19, 2022 | | Posted in Newsletter

Human evolution
“A new study by a team of researchers from Israel and Ghana has brought the first evidence of nonrandom [MORE]

A Gene Bypass

June 29, 2021 | | Posted in Newsletter

Bypasing gene mutations
“We [biologists and biochemists at Penn State] have developed a novel gene correction strategy, Co-opting Regulation Bypass Repair [MORE]

Reengineering Sickle Cells

May 5, 2015 | | Posted in Newsletter

Sickle Cell Disease
It is no more than a reversal of an A and T base pair in a point on [MORE]