CRISPR-Cas9 In Vivo Gene Editing for Transthyretin Amyloidosis
“Transthyretin amyloidosis . . . is a life-threatening disease characterized by progressive accumulation [MORE]
Regeneron Biorepository of Knockouts
In 2007, the Nobel Prize in Physiology or Medicine went to three scientists (Oliver Smithies, Martin Evans, [MORE]