POSTS TAGGED AS gene therapy

Organ on a Chip Technology

Game-changing Technology- Your Organs Can Now be Reproduced on a Chip
“A revolutionary aspect of this technology is that different organ-chips [MORE]

Gene Therapy for Muscle Loss

Myogenic tissue nanotransfection improves muscle torque recovery following following VLM
“This research work tests tissue nanotransfection (TNT) based gene therapy as [MORE]

“The Most Expensive Medicine in History”

New $2.8-million gene therapy becomes most expensive medicine in history
“The US Food and Drug Administration (FDA) has approved the first [MORE]

Bigger Cargo Carriers for Gene Therapy

Gene therapy delivered via  a high-capacity baculovirus
“Here we [University of Bristol, UK] exploit the unmatched heterologous DNA cargo capacity of [MORE]

Altering Gene Expression with Gold Nanorods and an NIR Laser

Altering Gene Expression with Gold Nanorods and an NIR Laser
Japanese scientists have used lipid coated gold nanorods to deliver a [MORE]

CRISPR Skin Grafts Instead of Insulin Injections

Engineered epidermal progenitor cells can correct diet-Induced obesity and diabetes
Researchers at the University of Chicago have used CRISPR gene editing [MORE]

Gene Editing of Endothelial Cells

Gene Editing of Endothelial Cells
“To target endothelium for robust genome editing, we developed poly(ethylene glycol) methyl ether-block-poly(lactide-co-glycolide) (PEG-b-PLGA) copolymer-based nanoparticle [MORE]

Logic-Gated Gene Therapy

Logic-Gated Gene Therapy
“Borrowing a concept from computation, scientists at ETH Zurich created genetic “logic gates” that can differentiate between tumor [MORE]

Twin Prime Editing in Gene Therapy

New prime editing system inserts entire genes
Researchers at the Broad Institute of MIT and Harvard . . . describes “ [MORE]

“Toehold” Switches for RNA Expression

RNA-responsive elements for eukaryotic translational control
In this piece, researchers at the Wyss Institute “. . .  introduce eukaryotic toehold switches [MORE]

Gene Therapy for Sight Restoration (mice)

Gene Therapy for Sight Restoration in mice
“After performing electrophysiological extracellular recordings and two-photon calcium imaging of reprogrammed cells in vivo [MORE]

Muscle-Tropic Capsids for Gene Transfer

Graphical abstract
“Here, we [scientists at the Broad Institute-MIT/Harvard] developed the DELIVER (directed evolution of AAV capsids leveraging in vivo expression [MORE]

SEND (Selective Endogenous eNcapsidation for Cellular Delivery)

mRNA gene therapy with a human protein
For a generation, gene therapy has relied on viral vectors to deliver a transgene.  [MORE]

Gene Transfer with an Optic Adeno-Associated Viral Vector

Design and mode of function of the light-controlled viral transduction system
German and Chinese bioengineers have used “an adeno-associated viral (AAV) [MORE]