POSTS TAGGED AS gene therapy

Gene Therapy for Rare Form of SCID

Lentiviral Gene Therapy for Artemis-Deficient SCID
“The DNA-repair enzyme Artemis is essential for rearrangement of T- and B-cell receptors. Mutations in [MORE]

2022’s Medical Milestones

Global effort realizes first 100% complete sequence of human genome
“The Human Genome Project has been running for decades, famously publishing [MORE]

Gender Modeling of Sex Differences

Modeling sex differences in humans using isogenic induced pluripotent stem cells
“In this work we [at Hebrew University, Jerusalem] developed a [MORE]

Gel-Delivered Topical Gene Therapy

Five-year-old Rowan Millner has dystrophic epidermolysis bullosa
From Stanford University:  “People with recessive dystrophic epidermolysis bullosa have a genetic mutation that [MORE]

Base-Editing Gene Therapy Cures a Child’s Incurable Leukemia

Teenager’s “incurable” leukemia cured by new base editing gene therapy
“A teenager in the UK has become the first person to [MORE]

Organ on a Chip Technology

Game-changing Technology- Your Organs Can Now be Reproduced on a Chip
“A revolutionary aspect of this technology is that different organ-chips [MORE]

Gene Therapy for Muscle Loss

Myogenic tissue nanotransfection improves muscle torque recovery following following VLM
“This research work tests tissue nanotransfection (TNT) based gene therapy as [MORE]

“The Most Expensive Medicine in History”

New $2.8-million gene therapy becomes most expensive medicine in history
“The US Food and Drug Administration (FDA) has approved the first [MORE]

Bigger Cargo Carriers for Gene Therapy

Gene therapy delivered via  a high-capacity baculovirus
“Here we [University of Bristol, UK] exploit the unmatched heterologous DNA cargo capacity of [MORE]

Altering Gene Expression with Gold Nanorods and an NIR Laser

Altering Gene Expression with Gold Nanorods and an NIR Laser
Japanese scientists have used lipid coated gold nanorods to deliver a [MORE]

CRISPR Skin Grafts Instead of Insulin Injections

Engineered epidermal progenitor cells can correct diet-Induced obesity and diabetes
Researchers at the University of Chicago have used CRISPR gene editing [MORE]

Gene Editing of Endothelial Cells

Gene Editing of Endothelial Cells
“To target endothelium for robust genome editing, we developed poly(ethylene glycol) methyl ether-block-poly(lactide-co-glycolide) (PEG-b-PLGA) copolymer-based nanoparticle [MORE]

Logic-Gated Gene Therapy

Logic-Gated Gene Therapy
“Borrowing a concept from computation, scientists at ETH Zurich created genetic “logic gates” that can differentiate between tumor [MORE]

Twin Prime Editing in Gene Therapy

New prime editing system inserts entire genes
Researchers at the Broad Institute of MIT and Harvard . . . describes “ [MORE]