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POSTS TAGGED AS beta thalassemia

“The Most Expensive Medicine in History”

November 8, 2022 | | Posted in Newsletter

New $2.8-million gene therapy becomes most expensive medicine in history
“The US Food and Drug Administration (FDA) has approved the first [MORE]

Gene Editing Shows Long Term Efficacy forBeta Thalassemia and Sickle Cell Disease

August 23, 2022 | | Posted in Newsletter

Sickle Cell Anemia
“In a late-breaking abstract presented at the European Hematology Association (EHA) Congress, a group of researchers that includes [MORE]

Another Win for CRISPR

October 26, 2021 | | Posted in Newsletter

CRISPR therapy for rare blood diseases
“Back in 2019 the first CRISPR human clinical trials kicked off in the United States. [MORE]

“Chemical Surgery” to Remove Single Point Mutations in DNA

November 14, 2017 | | Posted in Newsletter

Base Editing
CRISPR-Cas9 gene editing is the new tool in the box of molecular surgeons, but this method deletes multiple bases [MORE]